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Main
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Note: This record shows only 22 elements of the WHO Trial Registration Data Set. To view changes that have been made to the source record, or for additional information about this trial, click on the URL below to go to the source record in the primary register. |
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Register:
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ClinicalTrials.gov |
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Last refreshed on:
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12 December 2020 |
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Main ID: |
NCT02968953 |
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Date of registration:
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16/11/2016 |
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Prospective Registration:
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Yes |
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Primary sponsor: |
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Public title:
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Treatment With UX007 for a Single Patient With GLUT1 Deficiency Syndrome
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Scientific title:
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Treatment With UX007 (Triheptanoin) for a Single Patient (ERS) With Glucose Transporter 1 (GLUT1) Deficiency Syndrome |
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Date of first enrolment:
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March 17, 2017 |
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Target sample size:
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Recruitment status: |
No longer available |
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URL:
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https://clinicaltrials.gov/show/NCT02968953 |
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Study type:
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Expanded Access |
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Study design:
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Phase:
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Countries of recruitment
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United States
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Contacts
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Name:
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Gerard Vockley, MD, PhD |
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Address:
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Telephone:
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Email:
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Affiliation:
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University of Pittsburgh |
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Key inclusion & exclusion criteria
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Inclusion Criteria:
- This treatment plan is intended for the use of UX007 (triheptanoin) in the treatment
of a single patient with Glucose Transporter 1 (GLUT1) Deficiency Syndrome.
Exclusion Criteria:
- Not applicable as study only includes one patient.
Age minimum:
3 Years
Age maximum:
N/A
Gender:
Female
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Health Condition(s) or Problem(s) studied
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Glucose Transporter 1 Deficiency Syndrome
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Intervention(s)
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Drug: Triheptanoin
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Secondary ID(s)
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PRO16060524
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Source(s) of Monetary Support
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Please refer to primary and secondary sponsors
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Results
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Results available:
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Date Posted:
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Date Completed:
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URL:
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