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Main
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Note: This record shows only 22 elements of the WHO Trial Registration Data Set. To view changes that have been made to the source record, or for additional information about this trial, click on the URL below to go to the source record in the primary register. |
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Register:
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ClinicalTrials.gov |
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Last refreshed on:
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19 February 2015 |
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Main ID: |
NCT01760564 |
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Date of registration:
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02/01/2013 |
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Prospective Registration:
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No |
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Primary sponsor: |
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Public title:
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Application of Miglustat in Patients With Niemann-Pick Type C
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Scientific title:
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Application of Miglustat in Patients With Niemann-Pick Type C |
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Date of first enrolment:
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January 2008 |
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Target sample size:
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5 |
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Recruitment status: |
Completed |
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URL:
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http://clinicaltrials.gov/show/NCT01760564 |
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Study type:
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Interventional |
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Study design:
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Endpoint Classification: Safety Study, Intervention Model: Single Group Assignment, Masking: Open Label, Primary Purpose: Treatment
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Phase:
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Phase 3
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Countries of recruitment
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Taiwan
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Contacts
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Name:
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Whu-Liang Hwu, MD, PhD |
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Address:
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Telephone:
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Email:
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Affiliation:
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National Taiwan University Hospital |
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Key inclusion & exclusion criteria
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Inclusion Criteria:
- Confirm diagnosis of Niemann-Pick C disease
- Symptomatic including motor or mental symptoms
Exclusion Criteria:
- Unknown severe diarrhea for more than 7 day
- Allergy to miglustat
Age minimum:
N/A
Age maximum:
N/A
Gender:
Both
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Health Condition(s) or Problem(s) studied
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Niemann-Pick Disease Type C
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Intervention(s)
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Drug: Miglustat
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Primary Outcome(s)
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Swallowing
[Time Frame: 12th month]
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Secondary Outcome(s)
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Mental
[Time Frame: 12th month]
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Secondary ID(s)
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200802043M
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Source(s) of Monetary Support
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Please refer to primary and secondary sponsors
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Results
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Results available:
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Date Posted:
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Date Completed:
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URL:
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