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Main
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Note: This record shows only 22 elements of the WHO Trial Registration Data Set. To view changes that have been made to the source record, or for additional information about this trial, click on the URL below to go to the source record in the primary register. |
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Register:
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ClinicalTrials.gov |
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Last refreshed on:
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18 January 2016 |
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Main ID: |
NCT01203592 |
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Date of registration:
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15/09/2010 |
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Prospective Registration:
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No |
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Primary sponsor: |
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Public title:
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Efficacy of Albuterol in the Treatment of Congenital Myasthenic Syndromes
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Scientific title:
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Efficacy of Albuterol in the Treatment of Congenital Myasthenic Syndromes |
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Date of first enrolment:
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September 2010 |
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Target sample size:
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21 |
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Recruitment status: |
Completed |
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URL:
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https://clinicaltrials.gov/show/NCT01203592 |
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Study type:
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Interventional |
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Study design:
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Endpoint Classification: Efficacy Study, Intervention Model: Single Group Assignment, Masking: Open Label, Primary Purpose: Treatment
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Phase:
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Phase 1
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Countries of recruitment
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United States
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Contacts
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Name:
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Andrew G Engel, MD |
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Address:
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Telephone:
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Email:
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Affiliation:
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Mayo Clinic |
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Key inclusion & exclusion criteria
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Inclusion Criteria:
- Diagnosis of congenital myasthenic syndrome substantiated by typical clinical
history, seronegativity to AChR and MuSK, and evidence of a decremental EMG response.
Exclusion Criteria:
- Uncontrolled hypertension, arrhythmias, or other significant cardiac disease.
Age minimum:
2 Years
Age maximum:
N/A
Gender:
Both
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Health Condition(s) or Problem(s) studied
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Congenital Myasthenic Syndrome
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Intervention(s)
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Drug: Albuterol
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Primary Outcome(s)
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Name: Efficacy of albuterol in the treatment of congenital myasthenic syndromes
[Time Frame: 3 years]
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Secondary ID(s)
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10-004529
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Source(s) of Monetary Support
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Please refer to primary and secondary sponsors
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Results
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Results available:
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Date Posted:
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Date Completed:
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URL:
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