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Note: This record shows only the 20 elements of the WHO Trial Registration Data Set. To view changes that have been made to the source record, or for additional information about this trial, click on the URL below to go to the source record in the primary register.
Register: ClinicalTrials.gov
Last refreshed on: 17 October 2012
Main ID:  NCT01405742
Date of registration: 25/07/2011
Primary sponsor: University of Pittsburgh
Public title: Hemophilia Adult Prophylaxis Study
Scientific title: R34 Pilot Feasibility Randomized, Noninferiority, Cross-Over Trial of Once-Weekly vs. Thrice-Weekly Prophylaxis With Recombinant Factor VIII in Adults With Severe Hemophilia A
Date of first enrolment: July 2012
Target sample size: 20
Recruitment status: Recruiting
URL:  http://clinicaltrials.gov/show/NCT01405742
Study type:  Interventional
Study design:  Allocation: Randomized, Endpoint Classification: Safety/Efficacy Study, Intervention Model: Crossover Assignment, Masking: Open Label, Primary Purpose: Treatment  
Countries of recruitment
United States
Contacts
Name:   Margaret V. Ragni, MD, MPH
Address: 
Telephone: 412-209-7288
Email: ragni@dom.pitt.edu
Affiliation: 
Name:   Margaret V. Ragni, MD, MPH
Address: 
Telephone:
Email:
Affiliation:  University of Pittsburgh
Key inclusion & exclusion criteria

Inclusion Criteria:

- Adult males 18 years or older

- Severe hemophilia A (F.VIII < 0.01 U/ml)

- At least 150 exposure days to F.VIII products

- No detectable inhibitor

- No history of allergic reaction

- Platelets at least 150,000/ul

- If HIV(+), CD4 at least 200/ul, HIV-VL <48 copies/ml,and cART compliant

- If HCV(+), no splenomegaly,varices,GI bleed,ascites,edema,encephalopathy

- Willingness to comply with cross-over design, randomization schema

- Willingness to keep a personal diary of bleeding frequency and factor use

- Willingness to make every 3 month visits, coagulation testing at wks 2, 28

Exclusion Criteria:

- Acquired hemophilia

- Any bleeding disorder other than hemophilia A

- Presence of an inhibitor to factor VIII

- Historic platelet count < 100,000

- Use of experimental drugs

- Surgery anticipate in the next 52 weeks

- Symptomatic HCV(splenomegaly,varices,GI bleed,ascites,edema,encephalopathy)

- Symptomatic HIV(CD4<200/ul or HIV VL 48 or more copy/ml,cART noncompliant)

- Life expectancy less than 5 years

- Investigational drug or study within 4 weeks prior to study

- Inability to comply with study requirements



Age minimum: 18 Years
Age maximum: N/A
Gender: Male
Health Condition(s) or Problem(s) studied
Severe Hemophilia A
Intervention(s)
Drug: Recombinant factor VIII
Primary Outcome(s)
The primary outcome measure is bleeding frequency. [Time Frame: The time frame is 52 weeks per subject.]
Secondary Outcome(s)
A secondary outcome is inter-dose hypocoagulability by thrombin generation. [Time Frame: The time frame is 52 weeks per subject.]
A secondary outcome measure is F.VIII and inhibitor formation. [Time Frame: The time frame is 52 weeks per subject.]
A secondary outcome measure is factor usage and cost. [Time Frame: The time frame is 52 weeks per subject.]
A secondary outcomes is joint range of motion. [Time Frame: The time frame is 52 weeks per subject.]
Secondary ID(s)
PRO10020178
Source(s) of Monetary Support
Please refer to primary and secondary sponsors
Secondary Sponsor(s)
National Heart, Lung, and Blood Institute (NHLBI)
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