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Main
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Note: This record shows only 22 elements of the WHO Trial Registration Data Set. To view changes that have been made to the source record, or for additional information about this trial, click on the URL below to go to the source record in the primary register. |
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Register:
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ClinicalTrials.gov |
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Last refreshed on:
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12 December 2020 |
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Main ID: |
NCT01862042 |
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Date of registration:
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20/07/2012 |
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Prospective Registration:
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No |
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Primary sponsor: |
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Public title:
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Palliative Care in Spinal Muscular Atrophy (SMA) 1
ASI1 |
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Scientific title:
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Evaluation of Palliative and Supportive Care for Spinal Muscular Atrophy (SMA) Type 1 Patients |
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Date of first enrolment:
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June 2012 |
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Target sample size:
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39 |
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Recruitment status: |
Completed |
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URL:
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https://clinicaltrials.gov/show/NCT01862042 |
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Study type:
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Interventional |
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Study design:
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Allocation: N/A. Intervention model: Single Group Assignment. Primary purpose: Supportive Care. Masking: None (Open Label).
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Phase:
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N/A
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Countries of recruitment
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France
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Contacts
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Name:
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Isabelle Desguerre, MD, PhD |
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Address:
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Telephone:
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Email:
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Affiliation:
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Necker Hospital |
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Key inclusion & exclusion criteria
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Inclusion Criteria:
- SMA type 1 under 1 an
- Genetic confirmation
Exclusion Criteria:
- No genetic confirmation
- SMA type 1 over 1 year
Age minimum:
N/A
Age maximum:
1 Year
Gender:
All
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Health Condition(s) or Problem(s) studied
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Spinal Muscular Atrophy 1
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Intervention(s)
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Other: Follow-up diary and questionnaire
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Primary Outcome(s)
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%O2
[Time Frame: until 2 years]
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Secondary Outcome(s)
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Qualitative evaluation of the practices of care
[Time Frame: until 2 years]
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Evaluation of orthopedic facilities
[Time Frame: until 2 years]
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Evaluation of comfort
[Time Frame: until 2 years]
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Evaluation of nutritional status
[Time Frame: until 2 years]
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Secondary ID(s)
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P110135
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2012-A00024-39
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Source(s) of Monetary Support
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Please refer to primary and secondary sponsors
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Results
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Results available:
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Date Posted:
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Date Completed:
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URL:
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