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Main
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Note: This record shows only 22 elements of the WHO Trial Registration Data Set. To view changes that have been made to the source record, or for additional information about this trial, click on the URL below to go to the source record in the primary register. |
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Register:
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ClinicalTrials.gov |
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Last refreshed on:
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16 December 2017 |
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Main ID: |
NCT03045042 |
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Date of registration:
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27/01/2017 |
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Prospective Registration:
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Yes |
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Primary sponsor: |
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Public title:
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Search for Serum/Plasma Biomarkers in Pompe's Disease
BIOPOMPE |
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Scientific title:
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Search for Serum/Plasma Biomarkers in Pompe's Disease |
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Date of first enrolment:
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April 2017 |
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Target sample size:
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35 |
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Recruitment status: |
Not yet recruiting |
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URL:
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https://clinicaltrials.gov/show/NCT03045042 |
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Study type:
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Observational |
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Study design:
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Phase:
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N/A
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Countries of recruitment
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Spain
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Contacts
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Name:
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Eduard Gallardo, PhD |
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Address:
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Telephone:
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+349355657692 |
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Email:
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egallardo@gmail.com |
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Affiliation:
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Name:
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Eduard Gallardo, PhD |
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Address:
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Telephone:
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9355657682 |
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Email:
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egallardo@santpau.cat |
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Affiliation:
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Key inclusion & exclusion criteria
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Inclusion Criteria:
- Genetic confirmation of Pompe disease
Exclusion Criteria:
- Pregnancy
Age minimum:
2 Years
Age maximum:
N/A
Gender:
All
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Health Condition(s) or Problem(s) studied
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Pompe Disease
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Late Onset Pompe Disease
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Intervention(s)
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Drug: Enzyme Replacement Agent
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Primary Outcome(s)
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MicroRNA in serum samples
[Time Frame: Baseline]
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Secondary Outcome(s)
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Changes in microRNA concentration
[Time Frame: One year period]
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Muscle function test
[Time Frame: Baseline and one year]
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Whole body muscle MRI
[Time Frame: Baseline a and one year]
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Secondary ID(s)
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IIBSP-BIO-2017-02
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GZ-2015-11342
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Source(s) of Monetary Support
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Please refer to primary and secondary sponsors
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Results
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Results available:
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Date Posted:
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Date Completed:
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URL:
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